
Episode #8
Gene Therapy Is Here! Are You Ready?
<p>Send us Fan Mail</p><p>We sit down with hematology nurse practitioner Maya Bloomberg to cut through the noise around hemophilia gene therapy, including what it can realistically change and what it cannot. We talk durability, safety, access, and the human side of decision-making so patients and families can walk into care feeling informed and empowered. <br/><br/>• what gene therapy aims to do in hemophilia and why “cure” can mislead <br/>• how factor levels can rise, vary widely, and decline over time <br/>• eligibility basics, including AAV antibody testing and why redosing is limited <br/>• liver toxicity risk, frequent l...

